Novel Approaches for Mass Spectrometry Characterization of Highly Modified Synthetic RNA (On-Demand)

Curriculum

Course Description:
Over the last years, the demand of MS based structural characterization approaches in quality control of oligonucleotide based pharmaceuticals increased notably. Sense strand RNAs with >30 nucleotide building blocks and labile modifications such as N-acetylgalactosamine residues represent thereby a special challenge. We will present direct, robust and easy to use techniques for full nucleotide sequence characterization of highly modified single-stranded RNAs by top down tandem mass spectrometry. This will include a case study for an N-acetylgalactosamine modified RNA sense strand.
The approach can be applied on single strand level, as well as on siRNA duplex level in a single ESI-MS experiment. Based on this technique, we also developed an efficient and highly sophisticated LC-MS(/MS) workflow for the characterization of product-related impurities in oligonucleotides such as methylation as well as PS-PO and rC/rU substitution. This approach allows us to confidently predict the modification sites in oligonucleotide impurities to support process development with important structural information.

Who should participate:

  • QA Manager
  • QA Staff
  • QC Chemist
  • QC Manager
  • R&D
  • Regulatory
  • Student

The live version of this recording took place on during the USP Workshop on Therapeutic Peptides and Oligonucleotides:
Regulations and Quality Standards on March 2, 2022

Access Duration:
Access to this course expires 60 days from the date of registration or until you mark the course ‘Complete’ – whichever occurs first.

Speaker:
Giovanni Calderisi, Ph.D.
Project Chemist QC
Bachem Holding, Switzerland